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Sarepta Therapeutics Reports Positive Data from Part B of MOMENTUM Study of SRP-5051

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Duchenne Added to Minnesota’s Newborn Screening Panel

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CHMP Issues Negative Opinion for Renewal of Conditional Marketing Authorization for Translarna™ (ataluren) in Europe

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Astellas Releases Results of Discontinued Phase 1b Study of ASP0367

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PPMD Hosts 2024 Duchenne Healthcare Professionals Summit

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Introducing PPMD’s Gene Therapy Hub

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Join us at PPMD’s 30th year meetings and events

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PepGen Announces First Patient Dosed in CONNECT1-EDO51 Phase 2 Clinical Trial of PGN-EDO51

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Race to End Duchenne Celebrates Runners During Walt Disney World Marathon Weekend

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The Importance of Assisted Cough

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