Skip to main content

Blog

WATCH: Edgewise Therapeutics: A Novel Approach Designed to Protect Muscle in Becker (Webinar Recording)

...

Join Us for the Fall PPMD Lighthouse Workshops!

...

CDCC Spotlight: Helen DeVos Children’s Hospital

...

Sam’s Night Has Another Record-Breaking Year, Raising Over $1,400,000 for PPMD

...

WATCH: Supporting Families Through Decision Making (Webinar Recording)

...

WATCH: Affinity Duchenne™ and Affinity Beyond™: Updates on Investigational RGX-202 from REGENXBIO (Webinar Recording)

...

FibroGen announces discontinuation of LELANTOS-2 Open Label Extension

...

Santhera Receives Positive European Medicines Agency (EMA) CHMP Opinion Recommending Approval of Vamorolone in European Union

...

Finding and Accepting Help

...

What is Palliative Care? Understanding an additional layer of support

...