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Sarepta Announces Plans to Submit sNDAs for AMONDYS 45 and VYONDYS 53

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Sarepta Announces Initiation of Screening and Enrollment for ENDEAVOR Cohort 8 in Non-Ambulatory Individuals Living with Duchenne

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Community Comes Together on Capitol Hill: A Recap of PPMD’s 2026 Advocacy Conference

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Capricor Therapeutics Announces Positive Data from HOPE-3 Study of Deramiocel

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Solid Biosciences Shares Interim Positive Update on Phase 1/2 INSPIRE DUCHENNE Trial

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REGENXBIO Shares Positive Interim Data from Phase I/II AFFINITY DUCHENNE Trial of RGX-202

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Edgewise Announces Positive Long-Term Sevasemten Data

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Capricor Therapeutics Announces New PDUFA Date for Deramiocel

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PPMD and FED Announce 2026 Advocacy Leadership Awards Honoring Bipartisan Champions in Congress

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Advocates Unite in Washington to Advance Duchenne and Becker Policy, Mark 25th Anniversary of MD-CARE Act

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