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FDA Grants Approval to DUVYZAT™ (Givinostat)

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Italfarmaco Shares Updates Ahead of Givinostat PDUFA Date

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PPMD’s 2024 Advocacy Conference Brings Together Community to Support Progress in Fighting for Every Future

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WATCH: Sarepta Therapeutics – Data update from MOMENTUM study, SRP-5051 (Webinar Recording)

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PTC Therapeutics Announces Plans to Resubmit Translarna™ NDA to FDA

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WATCH: NS Pharma – Overview of New Exon Skipping Trials: Brogidirsen and NS-050/NCNP-03 (Webinar Recording)

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The Duchenne Registry Has a New Gene Therapy Survey!

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Join Us in Orlando for PPMD’s 30th Annual Conference

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Catalyst Pharmaceuticals Announces AGAMREE® Now Commercially Available in the U.S. for the Treatment of Duchenne

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REGENXBIO Shares New Positive Initial Efficacy Data From AFFINITY DUCHENNE Trial

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