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The Duchenne Registry Celebrates 15 Years of Data Collection

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Your Gift Today Funds ACTION

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Complete Your Registry Surveys and You Could Win Your Choice of a $150 Holiday Gift Card!

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Solid Biosciences Announces Completion of AavantiBio Acquisition & Update on Duchenne Pipeline Program

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Race Athlete Spotlight: Jason Hendry

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Sarepta Announces Biologics License Application (BLA) Accepted For Filing by the FDA for SRP-9001

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This Thanksgiving I am Grateful for You.

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PTC Shares Community Letter Updating on Activities To Bring Ataluren (Translarna) To US Patients

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Pfizer Announces First Participant Dosed in DAYLIGHT Phase 2 Gene Therapy Trial

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PPMD Provides Testimony During FDA CBER Meeting on Patient Perspectives on Gene Therapy Products

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