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NEW: Livestream with the PAAC

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GEMMABio Announces Duchenne Muscular Dystrophy Program, Shares Preclinical Data for Investigational Gene Therapy for Duchenne

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REGENXBIO Shares Topline Results from Pivotal Phase III AFFINITY DUCHENNE® Study of RGX-202

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Exercise in Dystrophinopathy: What Families Need to Know

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Solid Biosciences Doses First Participant in Phase 3 IMPACT DUCHENNE Clinical Trial Evaluating SGT-003 in Duchenne

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Momentum Continues: Duchenne Newborn Screening Advances Across the US

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Entrada Reports Positive Topline Results from Phase 1/2 ELEVATE-44-201 Study in Duchenne

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Catch up on PPMD Together: Philadelphia

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Advancing Duchenne Newborn Screening: A Collaborative Path Forward

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PTC Therapeutics Shares Updated Community Letter Regarding Ataluren

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