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The Future of Newborn Screening for Duchenne: Moving Forward After the ACHDNC’s Dissolution

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Recap: PPMD Together: Minneapolis, MN

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Watch: Avidity Biosciences – Topline Data from EXPLORE44® Clinical Trial (Webinar Recording)

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Dr. Peter Marks Resigns from FDA Center for Biologics Evaluation and Research

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Wave Life Sciences Announces Positive Data from FORWARD-53 Clinical Trial

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REGENXBIO Shares Positive Biomarker Data from AFFINITY DUCHENNE Trial of RGX-202 Gene Therapy

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Duchenne Secures $12.5 Million in CDMRP Funding for FY25: A Hard-Fought Victory in a Challenging Year

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A Safety Update on ELEVIDYS

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Key Updates from the 2025 MDA Clinical & Scientific Conference

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WATCH: Capricor Therapeutics – Update on Deramiocel for Cardiomyopathy in Patients with Duchenne (Webinar Recording)

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