Dyne Therapeutics Announces Positive Topline Results from Phase 1/2 DELIVER Trial of Z-Rostudirsen in Duchenne ...
Watch the Recording: Avidity Biosciences – EXPLORE44-OLE® Topline and Functional Data Presentation ...
Sarepta Announces FDA Approval to Begin ENDEAVOR Cohort 8 Dosing in Non-Ambulatory Individuals Living with Duchenne ...