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WATCH: ELEVIDYS: What This Means for You and Your Family (Webinar Recording)

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Join our 2023 Coach to Cure MD team!

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Duchenne Newborn Screening milestone—first state with universal newborn screening for Duchenne!

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Catch up on what’s happening at PPMD’s 2023 Annual Conference: Day 3

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Catch Up on What’s Happening at PPMD’s 2023 Annual Conference: Day 2

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Catch Up on What’s Happening at PPMD’s 2023 Annual Conference: Day 1

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Italfarmaco Group Announces NDA Accepted for Givinostat

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Edgewise Therapeutics announces positive topline 12-month data from EDG-5506 ARCH study

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FDA grants approval via accelerated approval pathway to ELEVIDYS: First-ever gene therapy for individuals with Duchenne ages 4-5

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Santhera announces exclusive North America license agreement with Catalyst Pharmaceuticals for vamorolone

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